Tag Archives: Sanfilippo

Anakinra shows promise in reducing symptoms in patients with Sanfilippo syndrome

As a neurodegenerative disease characterized by childhood-onset dementia, Sanfilippo syndrome causes enormous suffering in many ways, including pain, loss of speech, extreme agitation and anxiety, gastrointestinal symptoms, and profound sleep disturbances. In the absence of an approved treatment, clinical specialists have not yet had the ability to alleviate this suffering. Groundbreaking clinical research collaboration between […]